Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity-Reference-Cited by-同舟云学术

Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity

Published:2022-04-01 Issue:7-8 Volume:33 Page:371-388
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Tran Ngoc Tam¹²,Lecomte Emilie³,Saleun Sylvie³,Namkung Suk¹²^ORCID,Robin Cécile³,Weber Kristina⁴,Devine Eric³,Blouin Veronique³,Adjali Oumeya³,Ayuso Eduard³,Gao Guangping¹²⁵,Penaud-Budloo Magalie³,Tai Phillip W.L.¹²⁵^ORCID

Affiliation:

1. Horae Gene Therapy Center, UMass Chan Medical School, Worcester, Massachusetts, USA.

2. Department of Microbiology and Physiological Systems, UMass Chan Medical School, Worcester, Massachusetts, USA.

3. INSERM UMR 1089, University of Nantes, CHU of Nantes, Nantes, France.

4. Pacific Biosciences, Inc., Menlo Park, California, USA.

5. Li Weibo Institute of Rare Diseases Research; UMass Chan Medical School, Worcester, Massachusetts, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2022.050

Reference68 articles.

1. The clinical landscape for AAV gene therapies

2. Recombinant Adeno-Associated Virus Gene Therapy in Light of Luxturna (and Zolgensma and Glybera): Where Are We, and How Did We Get Here?

3. Pharmaceutical Development of AAV-Based Gene Therapy Products for the Eye

4. Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

5. Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union

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