1. Baylor College of Medicine, Dept. of Molecular and Human Genetics, Houston, TX 77030
2. San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), I-20132 Milan, Italy and Centro per la Diagnosi e Cura della Malattia di Gaucher e le Malattie Congenite del Metabolismo, I.R.C.C.S. Burlo Garofolo, 34137 Trieste, Italy
3. San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), I-20132 Milan, Italy and Genera SpA, I-20132 Milan, Italy
4. Deptartment of Pediatrics, Gifu University School of Medicine, 500 Gifu, Japan and E.A. Doisy Dept. of Biochemistry and Molecular Biology, St. Louis University School of Medicine, St. Louis, MO 63104
5. Deptartment of Pediatrics, Gifu University School of Medicine, 500 Gifu, Japan
6. Dipartimento di Biotecnologie e Bioscienze, Università di Milano-Bicocca, I-20126 Milan, Italy
7. San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), I-20132 Milan, Italy