1. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Surgery, University of Pennsylvania, Philadelphia, PA 19104
2. Department of Pediatrics, University of Pennsylvania, Philadelphia, PA 19104 and Children's Hospital of Philadelphia, Philadelphia, PA 19104
3. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
4. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Medicine, University of Pennsylvania, Philadelphia, PA 19104
5. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Radiology, University of Pennsylvania, Philadelphia, PA 19104
6. Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA 19104
7. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Biostatistics and Epidemiology, University of Pennsylvania, Philadelphia, PA 19104
8. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104
9. Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104; Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104 and Department of Medicine, University of Pennsylvania, Philadelphia, PA 19104
10. Department of Pediatrics, University of Pennsylvania, Philadelphia, PA 19104; Children's Hospital of Philadelphia, Philadelphia, PA 19104 and George Washington University School of Medicine and Health Sciences and Children's National Medical Center, Washington, DC 20008