Improving Molecular and Histopathology in Diaphragm Muscle of the Double Transgenic ACTA1-MCM/FLExDUX4 Mouse Model of FSHD with Systemic Antisense Therapy-Reference-Cited by-同舟云学术

Improving Molecular and Histopathology in Diaphragm Muscle of the Double Transgenic ACTA1-MCM/FLExDUX4 Mouse Model of FSHD with Systemic Antisense Therapy

Published:2022-09-01 Issue:17-18 Volume:33 Page:923-935
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Lu-Nguyen Ngoc¹^ORCID,Malerba Alberto¹^ORCID,Antoni Pineda Marina¹,Dickson George¹,Popplewell Linda¹

Affiliation:

1. Department of Biological Sciences, Centre for Biomedical Sciences, School of Life Sciences and the Environment, Royal Holloway University of London, Egham, United Kingdom.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2021.251

Reference71 articles.

1. Facioscapulohumeral muscular dystrophy: epidemiological and molecular study in a north-east Italian population sample

2. Population-based incidence and prevalence of facioscapulohumeral dystrophy

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5. Facioscapulohumeral Muscular Dystrophy: Update on Pathogenesis and Future Treatments

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