Design and Application of Bispecific Splice-Switching Oligonucleotides-Reference-Cited by-同舟云学术

Design and Application of Bispecific Splice-Switching Oligonucleotides

Published:2014-02 Issue:1 Volume:24 Page:13-24
ISSN:2159-3337
Container-title:Nucleic Acid Therapeutics
language:en
Short-container-title:Nucleic Acid Therapeutics

Author:

Bestas Burcu¹,McClorey Graham²,Tedebark Ulf¹³,Moreno Pedro M.D.¹,Roberts Thomas C.²⁴,Hammond Suzan M.²,Smith C.I. Edvard¹,Wood Matthew J.A.²,Andaloussi Samir EL¹²

Affiliation:

1. Department of Laboratory Medicine, Karolinska Institutet, Huddinge, Sweden.

2. Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford, United Kingdom.

3. GE Healthcare Bio-Sciences AB, Uppsala, Sweden.

4. Department of Molecular and Experimental Medicine, The Scripps Research Institute, La Jolla, California.

Publisher

Mary Ann Liebert Inc

Subject

Drug Discovery,Genetics,Molecular Biology,Molecular Medicine,Biochemistry

Link

http://www.liebertpub.com/doi/pdf/10.1089/nat.2013.0462

Reference49 articles.

1. Overview on DMD Exon Skipping

2. Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

3. Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More Sense

4. Exploring the Frontiers of Therapeutic Exon Skipping for Duchenne Muscular Dystrophy by Double Targeting within One or Multiple Exons

5. Antisense oligonucleotide induced exon skipping and the dystrophin gene transcript: cocktails and chemistries

Cited by 5 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Toward the therapeutic application of small interfering RNA bioconjugates in the central nervous system;Handbook of Innovations in Central Nervous System Regenerative Medicine;2020

2. Oligonucleotide Therapies: The Past and the Present;Human Gene Therapy;2015-08

3. Current Understanding of Molecular Pathology and Treatment of Cardiomyopathy in Duchenne Muscular Dystrophy;Molecules;2015-05-15

4. Bi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy;Nucleic Acids Research;2014-12-02

5. Antisense-Mediated Exon Skipping: Networking to Meet Opportunities and to Overcome Challenges;Nucleic Acid Therapeutics;2014-02