Lentiviral-Mediated Gene Transfer to the Sheep Brain: Implications for Gene Therapy in Batten Disease-Reference-Cited by-同舟云学术

Lentiviral-Mediated Gene Transfer to the Sheep Brain: Implications for Gene Therapy in Batten Disease

Published:2011-08 Issue:8 Volume:22 Page:1011-1020
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Linterman Kathryn S.¹²,Palmer David N.³,Kay Graham W.³,Barry Lucy A.³,Mitchell Nadia L.³,McFarlane Robin G.³,Black Michael A.¹,Sands Mark S.⁴,Hughes Stephanie M.¹²

Affiliation:

1. Department of Biochemistry, School of Medical Sciences, University of Otago, Dunedin 9054, New Zealand.

2. Brain Health Research Centre, University of Otago, Dunedin 9054, New Zealand.

3. Faculty of Agriculture and Life Sciences, Lincoln University, Lincoln 7647, New Zealand.

4. Division of Oncology, Washington University School of Medicine, St. Louis, MO 63110.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2011.026

Reference51 articles.

1. Magnetic Resonance Imaging-Guided Delivery of Adeno-Associated Virus Type 2 to the Primate Brain for the Treatment of Lysosomal Storage Disorders

2. Lentiviral Overexpression of GRK6 Alleviates l -Dopa–Induced Dyskinesia in Experimental Parkinson’s Disease

3. Comparison of Five Retrovirus Vectors Containing the Human IL-2 Receptor γ Chain Gene for Their Ability to Restore T and B Lymphocytes in the X-Linked Severe Combined Immunodeficiency Mouse Model

4. Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

5. Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells

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