Genome-Scale Analysis of Cellular Restriction Factors That Inhibit Transgene Expression from Adeno-Associated Virus Vectors-Reference-Cited by-同舟云学术

Genome-Scale Analysis of Cellular Restriction Factors That Inhibit Transgene Expression from Adeno-Associated Virus Vectors

Published:2023-04-27 Issue:4 Volume:97 Page:
ISSN:0022-538X
Container-title:Journal of Virology
language:en
Short-container-title:J Virol

Author:

Ngo Ashley M.¹,Puschnik Andreas S.¹^ORCID

Affiliation:

1. Chan Zuckerberg Biohub, San Francisco, California, USA

Abstract

Recombinant AAV (rAAV) vectors have been successfully developed for the treatment of genetic diseases. The therapeutic strategy often involves the replacement of a defective gene by the expression of a functional copy from the rAAV vector genome.

Publisher

American Society for Microbiology

Subject

Virology,Insect Science,Immunology,Microbiology

Link

https://journals.asm.org/doi/pdf/10.1128/jvi.01948-22

Reference52 articles.

1. Nucleotide sequence and organization of the adeno-associated virus 2 genome

2. AAV-Mediated Gene Therapy for Research and Therapeutic Purposes

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5. Emerging Issues in AAV-Mediated In Vivo Gene Therapy

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1. Genome-wide CRISPR screenings identified SMCHD1 as a host-restricting factor for AAV transduction;PLOS Pathogens;2024-07-08

2. Epigenetic Restriction Factors (eRFs) in Virus Infection;Viruses;2024-01-25

3. Understanding and Tackling Immune Responses to Adeno-Associated Viral Vectors;Human Gene Therapy;2023-09-01