Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I-Reference-Cited by-同舟云学术

Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I

Published:2011-03 Issue:3 Volume:19 Page:450-460
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Osborn Mark J,McElmurry Ron T,Lees Christopher J,DeFeo Anthony P,Chen Zhi-Ying,Kay Mark A,Naldini Luigi,Freeman Gordon,Tolar Jakub,Blazar Bruce R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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