A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell line
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/3300793.pdf
Reference35 articles.
1. Crystal R et al. The α1-antitrypsin gene and its mutations: clinical consequences and strategies for therapy Chest 1989 95: 196–208
2. Long G et al. Complete sequence of the cDNA for human α1 antitrypsin and the gene for the S variant J Biochem 1984 23: 4828–4837
3. Hubbard R, Crystal R . α1-Antitrypsin deficiency Am J Med 1988 85: 52–62
4. Crystal RG . The α1 antitrypsin gene and its deficiency states Trends Genet 1989 5: 411–417
5. Errickson S, Carlson S, Velez R . Risk of cirrhosis and primary liver cancer in α1-antitrypsin deficiency New Engl J Med 1986 314: 736–739
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