Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations-Reference-Cited by-同舟云学术

Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations

Published:2002-01 Issue:1 Volume:9 Page:53-63
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Matzner U,Hartmann D,Lüllmann-Rauch R,Coenen R,Rothert F,Månsson J-E,Fredman P,D'Hooge R,De Deyn PP,Gieselmann V

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/3301593.pdf

Reference30 articles.

1. Kolodny E.H., Fluharty A.L. . Metachromatic leukodystrophy and multiple sulfatase deficiency: sulfatide lipidosis Scriver CR, Beaudet AL, Sly WS, Valle D (eds); The Metabolic and Molecular Bases of Inherited Disease McGraw-Hill 1995 pp 2693–2740

2. Hess B. et al. Phenotype of arylsulfatase A-deficient mice: relationship to human metachromatic leukodystrophy Proc Natl Acad Sci USA 1996 93: 14821 14821

3. Gieselmann V. et al. Metachromatic leukodystrophy: molecular genetics and an animal model J Inher Metab Dis 1998 21: 564 564

4. D'Hooge R. et al. Neuromotor alterations and cerebellar deficits in aged arylsulfatase A-deficient transgenic mice Neurosci Lett 1999 273: 93 93

5. D'Hooge R. et al. Decline in brain stem auditory-evoked potentials coincides with loss of spiral ganglion cells in arylsulfatase A-deficient mice Brain Res 1999 847: 352 352

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