Lentiviral delivery of co-packaged Cas9 mRNA and a Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice-Reference-Cited by-同舟云学术

Lentiviral delivery of co-packaged Cas9 mRNA and a Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice

Published:2021-01-04 Issue:2 Volume:5 Page:144-156
ISSN:2157-846X
Container-title:Nature Biomedical Engineering
language:en
Short-container-title:Nat Biomed Eng

Author:

Ling Sikai,Yang Shiqi,Hu Xinde,Yin Di,Dai Yao,Qian Xiaoqing,Wang Dawei^ORCID,Pan Xiaoyong,Hong Jiaxu,Sun Xiaodong,Yang Hui^ORCID,Paludan Soren Riis^ORCID,Cai Yujia^ORCID

Publisher

Springer Science and Business Media LLC

Subject

Computer Science Applications,Biomedical Engineering,Medicine (miscellaneous),Bioengineering,Biotechnology

Link

http://www.nature.com/articles/s41551-020-00656-y.pdf

Reference76 articles.

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2. Kim, K. et al. Genome surgery using Cas9 ribonucleoproteins for the treatment of age-related macular degeneration. Genome Res. 27, 419–426 (2017).

3. van Diemen, F. R. et al. CRISPR/Cas9-mediated genome editing of herpesviruses limits productive and latent infections. PLoS Pathog. 12, e1005701 (2016).

4. Maeder, M. L. et al. Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10. Nat. Med. 25, 229–233 (2019).

5. Beyret, E. et al. Single-dose CRISPR-Cas9 therapy extends lifespan of mice with Hutchinson–Gilford progeria syndrome. Nat. Med. 25, 419–422 (2019).

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