An AAVrh10-CAG-CYP21-HA vector allows persistent correction of 21-hydroxylase deficiency in a Cyp21−/− mouse model
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
https://www.nature.com/articles/gt201710.pdf
Reference19 articles.
1. Gmyrek GA, New MI, Sosa RE, Poppas DP . Bilateral laparoscopic adrenalectomy as a treatment for classic congenital adrenal hyperplasia attributable to 21-hydroxylase deficiency. Pediatrics 2002; 109: E28.
2. Bruining H, Bootsma AH, Koper JW, Bonjer J, de Jong FH, Lamberts SWJ . Fertility and body composition after laparoscopic bilateral adrenalectomy in a 30-year-old female with congenital adrenal hyperplasia. J Clin Endocrinol Metab 2001; 86: 482–484.
3. Loechner KJ, McLaughlin JT, Calikoglu AS . Alternative strategies for the treatment of classical congenital adrenal hyperplasia: pitfalls and promises. Int J Pediatr Endocrinol 2010; 2010: 1–10.
4. Gastaud F, Bouvattier C, Duranteau L, Brauner R, Thibaud E, Kutten F et al. Impaired sexual and reproductive outcomes in women with classical forms of congenital adrenal hyperplasia. J Clin Endocrinol Metab 2007; 92: 1391–1396.
5. Riepe FG, Tatzel S, Sippell WG, Pleiss J, Krone N . Congenital adrenal hyperplasia: the molecular basis of 21-hydroxylase deficiency in H-2(aw18) mice. Endocrinology 2005; 146: 2563–2574.
Cited by 28 articles. 订阅此论文施引文献 订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献
1. Approach to the Child and Adolescent With Adrenal Insufficiency;The Journal of Clinical Endocrinology & Metabolism;2024-08-18
2. Genome editing in the adrenal gland: a novel strategy for treating congenital adrenal hyperplasia;Exploration of Endocrine and Metabolic Diseases;2024-07-09
3. AAV-delivered hepato-adrenal cooperativity in steroidogenesis: Implications for gene therapy for congenital adrenal hyperplasia;Molecular Therapy - Methods & Clinical Development;2024-06
4. Enhancing CAR-T cells: unleashing lasting impact potential with phytohemagglutinin activation in in vivo leukemia model;Cancer Gene Therapy;2023-12-14
5. Generation of glucocorticoid-producing cells derived from human pluripotent stem cells;Cell Reports Methods;2023-11
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3