Skeletal muscle-directed gene therapy: hijacking the fusogenic properties of muscle cells
Author:
Publisher
Springer Science and Business Media LLC
Subject
Cancer Research,Genetics
Link
https://www.nature.com/articles/s41392-023-01584-4.pdf
Reference5 articles.
1. Hindi, S.-M. et al. Enveloped viruses pseudotyped with mammalian myogenic cell fusogens target skeletal muscle for gene delivery. Cell 186, 2062–2077 (2023).
2. Isesele, P. O. & Mazurak, V. C. Regulation of skeletal muscle satellite cell differentiation by Omega-3 polyunsaturated fatty acids: a critical review. Front. Physiol. 12, 682091 (2021).
3. Liu, J., Koay, T. W., Maiakovska, O., Zayas, M. & Grimm, D. Progress in bioengineering of myotropic adeno-associated viral gene therapy vectors. Hum. Gene Ther. 34, 350–364 (2023).
4. Sampath, S. C., Sampath, S. C. & Millay, D. P. Myoblast fusion confusion: the resolution begins. Skelet. Muscle 8, 3 (2018).
5. Buchholz, C. J., Friedel, T. & Büning, H. Surface-engineered viral vectors for selective and cell type-specific gene delivery. Trends Biotechnol. 33, 777–790 (2015).
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