Antisense oligonucleotide therapy for spinocerebellar ataxia type 2-Reference-Cited by-同舟云学术

Antisense oligonucleotide therapy for spinocerebellar ataxia type 2

Published:2017-04-12 Issue:7650 Volume:544 Page:362-366
ISSN:0028-0836
Container-title:Nature
language:en
Short-container-title:Nature

Author:

Scoles Daniel R.,Meera Pratap,Schneider Matthew D.,Paul Sharan,Dansithong Warunee,Figueroa Karla P.,Hung Gene,Rigo Frank,Bennett C. Frank,Otis Thomas S.,Pulst Stefan M.

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/nature22044.pdf

Reference31 articles.

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2. Pulst, S. M., Nechiporuk, A. & Starkman, S. Anticipation in spinocerebellar ataxia type 2. Nat. Genet. 5, 8–10 (1993)

3. Dansithong, W. et al. Ataxin-2 regulates RGS8 translation in a new BAC-SCA2 transgenic mouse model. PLoS Genet. 11, e1005182 (2015)

4. Hansen, S. T., Meera, P., Otis, T. S. & Pulst, S. M. Changes in Purkinje cell firing and gene expression precede behavioral pathology in a mouse model of SCA2. Hum. Mol. Genet. 22, 271–283 (2013)

5. Pulst, S. M. Degenerative ataxias, from genes to therapies: The 2015 Cotzias Lecture. Neurology 86, 2284–2290 (2016)

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