Fludarabine increases nuclease-free AAV- and CRISPR/Cas9-mediated homologous recombination in mice-Reference-Cited by-同舟云学术

Fludarabine increases nuclease-free AAV- and CRISPR/Cas9-mediated homologous recombination in mice

Published:2022-04-07 Issue:8 Volume:40 Page:1285-1294
ISSN:1087-0156
Container-title:Nature Biotechnology
language:en
Short-container-title:Nat Biotechnol

Author:

Tsuji Shinnosuke^ORCID,Stephens Calvin J.,Bortolussi Giulia,Zhang Feijie,Baj Gabriele^ORCID,Jang Hagoon,de Alencastro Gustavo,Muro Andrés F.^ORCID,Pekrun Katja^ORCID,Kay Mark A.^ORCID

Funder

National Hemophilia Foundation

Dr. Ralph and Marian Falk Medical Research Trust

Publisher

Springer Science and Business Media LLC

Subject

Biomedical Engineering,Molecular Medicine,Applied Microbiology and Biotechnology,Bioengineering,Biotechnology

Link

https://www.nature.com/articles/s41587-022-01240-2.pdf

Reference57 articles.

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3. Wang, L., Wang, H., Bell, P., Mcmenamin, D. & Wilson, J. M. Brief report hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector. Hum. Gene Ther. 23, 533–539 (2011).

4. Wang, L. et al. AAV8-mediated hepatic gene transfer in infant rhesus monkeys (Macaca mulatta). Mol. Ther. 19, 2012–2020 (2012).

5. Cunningham, S. C., Dane, A. P., Spinoulas, A. & Alexander, I. E. Gene delivery to the juvenile mouse liver using AAV2/8 vectors. Mol. Ther. 16, 1081–1088 (2008).

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