Engineering and Characterization of an Enzyme Replacement Therapy for Classical Homocystinuria
Author:
Affiliation:
1. Department of Pediatrics, University of Colorado School of Medicine, Aurora, Colorado 80045, United States
2. Orphan Technologies Ltd., Rapperswil, CH-8640, Switzerland
Funder
American Heart Association
Orphan Technologies Ltd.
Publisher
American Chemical Society (ACS)
Subject
Materials Chemistry,Polymers and Plastics,Biomaterials,Bioengineering
Link
https://pubs.acs.org/doi/pdf/10.1021/acs.biomac.7b00154
Reference36 articles.
1. Methionine metabolism in mammals
2. Targeting Cystathionine Beta-Synthase Misfolding in Homocystinuria by Small Ligands: State of the Art and Future Directions
3. Structural insight into the molecular mechanism of allosteric activation of human cystathionine β-synthase byS-adenosylmethionine
4. Trypsin Cleavage of Human Cystathionine β-Synthase into an Evolutionarily Conserved Active Core: Structural and Functional Consequences
5. Domain Organization, Catalysis and Regulation of Eukaryotic Cystathionine Beta-Synthases
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1. Current and Novel Therapeutical Approaches of Classical Homocystinuria in Childhood With Special Focus on Enzyme Replacement Therapy, Liver-Directed Therapy and Gene Therapy;Journal of Clinical Medicine Research;2023-02
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