Brain Development in Infantile-Onset Pompe Disease Treated by Enzyme Replacement Therapy
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pediatrics, Perinatology and Child Health
Reference18 articles.
1. NERVOUS SYSTEM IN POMPEʼS DISEASE
2. The Natural Course of Infantile Pompe’s Disease: 20 Original Cases Compared With 133 Cases From the Literature
3. Towards a molecular therapy for glycogen storage disease type II (Pompe disease)
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