1. Dubowitz Neuromuscular Centre UCL Great Ormond Street Institute of Child Health London UK
2. NIHR Great Ormond Street Hospital Biomedical Research Centre UCL Great Ormond Street Institute of Child Health London UK
3. Population, Policy and Practice Research and Teaching Department UCL Great Ormond Street Institute of Child Health London UK
4. Department of Molecular Therapy National Institute of Neuroscience, National Center of Neurology and Psychiatry (NCNP) Kodaira Japan
5. Department of Cell and Developmental Biology University College London London UK
6. Centre for Genomics and Child Health, Blizard Institute, Barts and the London School of Medicine and Dentistry Queen Mary University of London London UK
7. The Francis Crick Institute London UK