Alternative designs for clinical trials in rare diseases
Author:
Publisher
Wiley
Subject
Genetics (clinical),Genetics
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1002/ajmg.c.31533/fullpdf
Reference97 articles.
1. Response times follow lognormal or gamma distribution in arthritis patients;Abrahamyan;J Clin Epidemiol,2010
2. A new toolkit for conducting clinical trials in rare disorders;Abrahamyan;J Popul Ther Clin Pharmacol,2014
3. Survival distributions impact the power of randomized placebo-phase design and parallel groups randomized clinical trials;Abrahamyan;J Clin Epidemiol,2011
4. Biomarkers and surrogate endpoints;Aronson;Br J Clin Pharmacol,2005
5. Case studies, single-subject research, and N of 1 randomized trials: Comparisons and contrasts. [Review] [22 refs];Backman;Am J Phys Med Rehabil,1999
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