Hematopoietic Stem cell transplantation and lentiviral vector‐based gene therapy for Krabbe's disease: Present convictions and future prospects-Reference-Cited by-同舟云学术

Hematopoietic Stem cell transplantation and lentiviral vector‐based gene therapy for Krabbe's disease: Present convictions and future prospects

Published:2016-09-17 Issue:11 Volume:94 Page:1152-1168
ISSN:0360-4012
Container-title:Journal of Neuroscience Research
language:en
Short-container-title:Journal of Neuroscience Research

Author:

Hu Peirong¹,Li Yedda²,Nikolaishvili‐Feinberg Nana³,Scesa Giuseppe⁴,Bi Yanmin¹,Pan Dao⁵⁶,Moore Dominic⁷,Bongarzone Ernesto R.⁴,Sands Mark S.²,Miller Ryan³⁸,Kafri Tal¹

Affiliation:

1. Gene Therapy Center and Department of Microbiology and ImmunologyUniversity of North Carolina at Chapel HillChapel Hill North Carolina

2. Department of Internal MedicineWashington University in St. Louis, School of MedicineSt Louis Missouri

3. Lineberger Comprehensive Cancer CenterUniversity of North Carolina at Chapel HillChapel Hill North Carolina

4. Department of Anatomy and Cell Biology, College of MedicineUniversity of Illinois ChicagoChicago Illinois

5. Division of Experimental Hematology and Cancer BiologyCincinnati Children's Hospital Medical CenterCincinnati Ohio

6. Department of PediatricsUniversity of CincinnatiCincinnati Ohio

7. Biostatistics Core Facility, UNC Lineberger Comprehensive Cancer Center, School of MedicineUniversity of North Carolina at Chapel HillChapel Hill North Carolina

8. Departments of Pathology and Laboratory Medicine and of Neurology, Neurosciences CenterUniversity of North Carolina at Chapel HillChapel Hill North Carolina

Funder

Legacy of Angels Foundation

National Institutes of Health

Publisher

Wiley

Subject

Cellular and Molecular Neuroscience

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/jnr.23847

Reference48 articles.

1. Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

2. Hematopoietic Cell Transplantation for Mucopolysaccharidosis Patients Is Safe and Effective: Results after Implementation of International Guidelines