1. Sarepta Therapeutics, Inc. Cambridge Massachusetts USA
2. Analysis Group, Inc. Boston Massachusetts USA
3. Boston Children's Hospital and Harvard Medical School Boston Massachusetts USA
4. University of California Davis Health System Sacramento California USA
5. Paediatric Neurology and Centro Clinico NeMO Catholic University and Policlinico Gemelli, Fondazione Policlinico Universitario Agostino Gemelli IRCSS Rome Italy
6. Centro Clinico NeMO Fondazione Policlinico Universitario Agostino Gemelli IRCSS Rome Italy
7. Dubowitz Neuromuscular Centre UCL Institute of Child Health and Great Ormond Street Hospital for Children London UK
8. Great Ormond Street Hospital London UK
9. NIHR Great Ormond Street Hospital Biomedical Research Centre London UK