Prolonged expression of a lysosomal enzyme in mouse liver afterSleeping Beauty transposon-mediated gene delivery: implications for non-viral gene therapy of mucopolysaccharidoses-Reference-Cited by-同舟云学术

Prolonged expression of a lysosomal enzyme in mouse liver afterSleeping Beauty transposon-mediated gene delivery: implications for non-viral gene therapy of mucopolysaccharidoses

Published:2007 Issue:5 Volume:9 Page:403-415
ISSN:1099-498X
Container-title:The Journal of Gene Medicine
language:en
Short-container-title:J. Gene Med.

Author:

Aronovich Elena L.,Bell Jason B.,Belur Lalitha R.,Gunther Roland,Koniar Brenda,Erickson David C. C.,Schachern Patricia A.,Matise Ilze,McIvor R. Scott,Whitley Chester B.,Hackett Perry B.

Publisher

Wiley

Subject

Genetics (clinical),Drug Discovery,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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5. Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome

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