Pharmacokinetics and Pharmacodynamics of the Small Interfering Ribonucleic Acid, Givosiran, in Patients With Acute Hepatic Porphyria
Author:
Affiliation:
1. Alnylam Pharmaceuticals Cambridge MA USA
Funder
Alnylam Pharmaceuticals
Publisher
Wiley
Subject
Pharmacology (medical),Pharmacology
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1002/cpt.1802
Reference21 articles.
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3. Patient Perspective on Acute Intermittent Porphyria with Frequent Attacks: A Disease with Intermittent and Chronic Manifestations
4. Acute hepatic porphyrias: Recommendations for evaluation and long-term management
5. Role of Delta-aminolevulinic Acid in the Symptoms of Acute Porphyria
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