Inherited retinal diseases: Therapeutics, clinical trials and end points

Inherited retinal diseases: Therapeutics, clinical trials and end points—A review

Published:2021-03-20 Issue:3 Volume:49 Page:270-288
ISSN:1442-6404
Container-title:Clinical & Experimental Ophthalmology
language:en
Short-container-title:Clin Experiment Ophthalmol

Author:

Georgiou Michalis¹²,Fujinami Kaoru¹²³⁴,Michaelides Michel¹²

Affiliation:

1. UCL Institute of Ophthalmology University College London London UK

2. Moorfields Eye Hospital NHS Foundation Trust London UK

3. Laboratory of Visual Physiology, Division of Vision Research National Institute of Sensory Organs, National Hospital Organization Tokyo Medical Center Tokyo Japan

4. Department of Ophthalmology Keio University School of Medicine Tokyo Japan

Funder

University of South Alabama

Retina UK

Wellcome Trust

A.G. Leventis Foundation

Alexander S. Onassis Public Benefit Foundation

University of Kentucky

National Institute for Health Research Biomedical Research Centre at Moorfields Eye Hospital NHS Foundation Trust and UCL Institute of Ophthalmology

Publisher

Wiley

Subject

Ophthalmology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/ceo.13917

Reference181 articles.

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4. Genetic Basis of Inherited Retinal Disease in a Molecularly Characterized Cohort of More Than 3000 Families from the United Kingdom

5. Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations

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