Gene therapy preferences and informed decision‐making: Results from a National Hemophilia Foundation Community Voices in research survey-Reference-Cited by-同舟云学术

Gene therapy preferences and informed decision‐making: Results from a National Hemophilia Foundation Community Voices in research survey

Published:2022-12-05 Issue:1 Volume:29 Page:51-60
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Limjoco Jacqueline¹,Calatroni Agustin²,Aristizabal Paula¹³⁴,Thornburg Courtney D.¹³

Affiliation:

1. Hemophilia and Thrombosis Treatment Center Rady Children's Hospital San Diego San Diego California USA

2. Rho Federal Systems Division Durham North Carolina USA

3. Department of Pediatrics University of California San Diego Health Sciences La Jolla California USA

4. Population Sciences, Disparities and Community Engagement University of California San Diego Moores Cancer Center and University of California San Diego Altman Clinical and Translational Research Institute Dissemination and Implementation Science Center La Jolla California USA

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.14706

Reference38 articles.

1. Emicizumab Prophylaxis in Patients Who Have Hemophilia A without Inhibitors

2. Concizumab: a novel anti-TFPI therapeutic for hemophilia

3. Targeting of antithrombin in hemophilia A or B with investigational siRNA therapeutic fitusiran‐Results of the phase 1 inhibitor cohort;Pasi KJ;JTH,2021

4. Recent advances in the treatment of hemophilia: a review;Marchesini E;Biologics,2021

5. An investigational RNAi therapeutic targeting antithrombin for the treatment of hemophilia A and B

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1. How clinicians and persons with hemophilia may approach shared decision-making;Expert Review of Hematology;2024-05-11

2. A multi-stakeholder collaborative approach to awareness, education and support needed in the haemophilia gene therapy patient journey – a report on insights from a European patient advisory board;The Journal of Haemophilia Practice;2024-01-01

3. Exploring patient and clinician perspectives on the benefits and risks of emerging therapies for the treatment of haemophilia: a qualitative study;The Journal of Haemophilia Practice;2024-01-01

4. Perspectives and perception of haemophilia gene therapy by French patients;Haemophilia;2023-12-06

5. Evaluating Gene Therapy as a Potential Paradigm Shift in Treating Severe Hemophilia;BioDrugs;2023-07-25