Electronic diaries in the management of haemophilia gene therapy: Perspective of an expert group from the German, Austrian and Swiss Society on Thrombosis and Haemostasis (GTH)-Reference-Cited by-同舟云学术

Electronic diaries in the management of haemophilia gene therapy: Perspective of an expert group from the German, Austrian and Swiss Society on Thrombosis and Haemostasis (GTH)

Published:2022-02-19 Issue:2 Volume:28 Page:264-269
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Miesbach Wolfgang¹^ORCID,Eichler Hermann²^ORCID,Holstein Katharina³,Holzhauer Susanne⁴,Klamroth Robert⁵^ORCID,Knöfler Ralf⁶,Male Christoph⁷,Olivieri Martin⁸^ORCID,Oldenburg Johannes⁹¹⁰^ORCID,Tiede Andreas¹¹^ORCID

Affiliation:

1. Department of Haemostaseology and Haemophilia Centre Medical Clinic 2 Institute of Transfusion Medicine University Hospital Frankfurt Frankfurt Germany

2. Institute of Clinical Haemostaseology and Transfusion Medicine Saarland University and University Hospital Homburg/Saar Germany

3. Haemophilia Center II. Medical Department University Medical Center Hamburg‐Eppendorf Hamburg Germany

4. Pediatric Hematology and Oncology Charité University Medicine Berlin Berlin Germany

5. Department for Internal Medicine – Vascular medcine and Haemostaseology Haemophilia Centre Vivantes Clinic imFriedrichshain Berlin Germany

6. Department of Paediatric Haemostaseology University Hospital Carl Gustav Carus Technical University Dresden Dresden Germany

7. Department of Paediatrics Medical University of Vienna Vienna Austria

8. Paediatric Haemostasis and Thrombosis Unit Paediatric Haemophilia Center Department of Paediatrics LMU Dr. von Hauner Children's Hospital University Hospital Munich Germany

9. Institute of Experimental Hematology and Transfusion Medicine Medical Faculty University Hospital Bonn University of Bonn Bonn Germany

10. Center for Rare Diseases Bonn (ZSEB) University Clinic Bonn Bonn Germany

11. Hannover Medical School Department of Hematology Hemostasis, Oncology and Stem Cell Transplantation Hannover Germany

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.14516

Reference18 articles.

1. Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A

2. Five Year Data Confirms Stable FIX Expression and Sustained Reductions in Bleeding and Factor IX Use Following AMT‐060 Gene Therapy in Adults with Severe or Moderate‐severe Hemophilia B [abstract];Miesbach W;Res Pract Thromb Haemost,2021

3. Adeno-Associated Mediated Gene Transfer for Hemophilia B:8 Year Follow up and Impact of Removing "Empty Viral Particles" on Safety and Efficacy of Gene Transfer

4. Scalable Production of AAV Vectors in Orbitally Shaken HEK293 Cells

5. AAV Production Using Baculovirus Expression Vector System

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1. Gene therapy for hemophilia—opportunities and risks;Deutsches Ärzteblatt international;2022-12-27

2. Gentherapie der Hämophilie: Empfehlung der Gesellschaft für Thrombose- und Hämostaseforschung (GTH);Hämostaseologie;2022-12-14