1. Division of Haematology/Oncology; Department of Paediatrics; Child Health Evaluative Sciences, Research Institute, Hospital for Sick Children; Toronto ON Canada
2. Indiana Hemophilia & Thrombosis Center; Indianapolis IN USA
3. University of Iowa Stead Family Children's Hospital; Iowa City IA USA
4. Center for Inherited Blood Disorders; Orange CA USA
5. University of Virginia Health System; Charlottesville VA USA
6. Walter Reed National Military Medical Center; Bethesda MD USA
7. University of Alberta Stollery Children's Hospital; Edmonton AB Canada
8. Rady Children's Hospital San Diego; San Diego CA USA
9. University Hospitals Rainbow Babies and Children's Hospital; Cleveland OH USA
10. Bioverativ Therapeutics, Inc.; Waltham MA USA
11. Trinity Partners LLC; Waltham MA USA
12. University of Michigan; Ann Arbor MI USA