Postmarketing safety and effectiveness of recombinant factor IX (nonacog alfa) in Japanese patients with haemophilia B

Author:

Fukutake Katsuyuki12,Taki Masashi3,Matsushita Tadashi4,Sakai Michio5,Takata Ami6,Yamaguchi Hiromi6,Karumori Toshiyuki6ORCID

Affiliation:

1. Department of Laboratory Medicine Tokyo Medical University Tokyo Japan

2. Department of Molecular Genetics of Coagulation Disorders Tokyo Medical University Tokyo Japan

3. Department of Pediatrics, St. Marianna University School of Medicine Yokohama City Seibu Hospital Yokohama Japan

4. Department of Transfusion Medicine Nagoya University Hospital Nagoya Japan

5. Department of Pediatrics University of Occupational and Environmental Health Kitakyushu Japan

6. Pfizer Japan Tokyo Japan

Funder

Pfizer Japan

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

Reference13 articles.

1. World Federation of Hemophilia. Report on the annual global survey 2016.http://www1.wfh.org/publications/files/pdf-1690.pdf. Accessed July 3 2018.

2. World Federation of Hemophilia. Guidelines for the Management of Hemophilia 2nd edition.http://www1.wfh.org/publications/files/pdf-1472.pdf. Accessed July 3 2018.

3. Medical and Scientific Advisory Council (MASAC). MASAC Recommendation Concerning Prophylaxis.https://www.hemophilia.org/sites/default/files/document/files/241Prophylaxis.pdf. Accessed July 3 2018.

4. Prophylaxis versus Episodic Treatment to Prevent Joint Disease in Boys with Severe Hemophilia

5. Update on treatment regimens: Prophylaxis versus on-demand therapy

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