A <scp>14‐step</scp> desensitization protocol for sebelipase alfa hypersensitivity in a patient with Wolman disease and secondary hemophagocytic lymphohistiocytosis-Reference-Cited by-同舟云学术

A 14‐step desensitization protocol for sebelipase alfa hypersensitivity in a patient with Wolman disease and secondary hemophagocytic lymphohistiocytosis

Published:2024-04 Issue:4 Volume:35 Page:
ISSN:0905-6157
Container-title:Pediatric Allergy and Immunology
language:en
Short-container-title:Pediatric Allergy Immunology

Author:

Nguyen Minh H. N.¹^ORCID,Bruening Rachel²,Abel Trent²,Lyons Shannon²,Denhardt Brenna³,Moore Jenna³,Sriaroon Panida¹,Hajirawala Monica¹,Kim Alexander Y.⁴^ORCID

Affiliation:

1. Division of Allergy and Immunology, Department of Pediatrics University of South Florida Morsani College of Medicine Tampa Florida USA

2. Department of Pharmacy Johns Hopkins All Children's Hospital St. Petersburg Florida USA

3. Nutritional Services Johns Hopkins All Children's Hospital St. Petersburg Florida USA

4. Division of Genetics, Department of Medicine Johns Hopkins All Children's Hospital St. Petersburg Florida USA

Publisher

Wiley

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/pai.14121

Reference10 articles.

1. Targeting Wolman Disease and Cholesteryl Ester Storage Disease: Disease Pathogenesis and Therapeutic Development

2. Enzyme replacement therapy and hematopoietic stem cell transplant: a new paradigm of treatment in Wolman disease

3. Wolman's disease and cholesteryl ester storage disorder: the phenotypic spectrum of lysosomal acid lipase deficiency

4. Wolman disease presenting with hemophagocytic lymphohistiocytosis syndrome and a novel LIPA gene variant: a case report and review of the literature

5. Rapid whole‐genome sequencing leading to specific treatment for two infants with haemophagocytic lymphohistiocytosis due to Wolman disease