Relationship Between Glucocerebrosidase Activity and Clinical Response to Enzyme Replacement Therapy in Patients With Gaucher Disease Type I-Reference-Cited by-同舟云学术

Relationship Between Glucocerebrosidase Activity and Clinical Response to Enzyme Replacement Therapy in Patients With Gaucher Disease Type I

Published:2018-03-30 Issue:1 Volume:123 Page:65-71
ISSN:1742-7835
Container-title:Basic & Clinical Pharmacology & Toxicology
language:en
Short-container-title:Basic Clin Pharmacol Toxicol

Author:

Gras-Colomer Elena¹²^ORCID,Martínez-Gómez María-Amparo¹²,Climente-Martí Mónica¹³,Fernandez-Zarzoso Miguel⁴,Almela-Tejedo Mercedes⁵,Giner-Galvañ Vicente⁶,Marcos-Rodríguez Jose-Antonio⁷,Rodríguez-Fernández Alicia⁸,Torralba-Cabeza Miguel-Ángel⁹,Merino-Sanjuan Matilde³¹⁰

Affiliation:

1. Department of Pharmacy; University Hospital Doctor Peset of Valencia; Valencia Spain

2. Foundation for the Promotion of Health and Biomedical Research of Valencia (FISABIO); Valencia Spain

3. Pharmacy and Pharmaceutical Technology; University of Valencia; Valencia Spain

4. Department of Hematology; University Hospital Doctor Peset of Valencia; Valencia Spain

5. Department of Pharmacy; Hospital Virgen de los Lirios of Alcoi; Alcoi Spain

6. Department of Internal Medicine; Hospital Virgen de los Lirios of Alcoi; Alcoi Spain

7. Department of Pharmacy; University Hospital Virgen Macarena; Seville Spain

8. Department of Hematology; University Hospital Virgen Macarena; Seville Spain

9. Deparment of Internal Medicine; University Clinical Hospital Lozano Blesa of Zaragoza; Zaragoza Spain

10. Molecular Recognition and Technological Development Institute; Mixed Unit Polytechnic University of Valencia; University of Valencia; Valencia Spain

Funder

Foundation for the Promotion of Health and Biomedical Research of Valencia, FISABIO

Publisher

Wiley

Subject

Pharmacology,Toxicology,General Medicine

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/bcpt.12977/fullpdf

Reference38 articles.

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3. The diagnosis of the adult type of Gaucher's disease and its carrier state by demonstration of deficiency of beta-glucosidase activity in peripheral blood leukocytes;Beutler;J Lab Clin Med,1970

4. The clinical course of treated and untreated Gaucher disease. A study of 45 patients;Beutler;Blood Cells Mol Dis,1995

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