Clinical advances in gene therapy updates on clinical trials of gene therapy in haemophilia-Reference-Cited by-同舟云学术

Clinical advances in gene therapy updates on clinical trials of gene therapy in haemophilia

Published:2019-07-08 Issue:5 Volume:25 Page:738-746
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Peyvandi Flora¹²^ORCID,Garagiola Isabella¹^ORCID

Affiliation:

1. Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center and Fondazione Luigi Villa Milan Italy

2. Department of Pathophysiology and Transplantation Università degli Studi di Milano Milan Italy

Publisher

Wiley

Subject

Genetics(clinical),Hematology,General Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.13816

Reference66 articles.

1. The past and future of haemophilia: diagnosis, treatments, and its complications

2. Future of coagulation factor replacement therapy

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4. Implantation of autologous skin fibroblast genetically modified to secrete clotting factor IX partially corrects the hemorrhagic tendencies in two hemophilia B patients;Qiu X;Chin Med J,1996

5. Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

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