Genotype-phenotype studies in infantile spinal muscular atrophy (SMA) type I in Germany: implications for clinical trials and genetic counselling
Author:
Publisher
Wiley
Subject
Genetics(clinical),Genetics
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1111/j.1399-0004.2009.01200.x/fullpdf
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4. In vivo activation of SMN in spinal muscular atrophy carriers and patients treated with valproate;Brichta;Ann Neurol,2006
5. Valproic acid treatment in six patients with spinal muscular atrophy;Tsai;Eur J Neurol,2007
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