Intracerebroventricular enzyme replacement therapy with β-galactosidase reverses brain pathologies due to GM1 gangliosidosis in mice-Reference-Cited by-同舟云学术

Intracerebroventricular enzyme replacement therapy with β-galactosidase reverses brain pathologies due to GM1 gangliosidosis in mice

Published:2020-09 Issue:39 Volume:295 Page:13532-13555
ISSN:0021-9258
Container-title:Journal of Biological Chemistry
language:en
Short-container-title:Journal of Biological Chemistry

Author:

Chen Joseph C.,Luu Amanda R.,Wise Nathan,Angelis Rolando De,Agrawal Vishal,Mangini Linley,Vincelette Jon,Handyside Britta,Sterling Harry,Lo Melanie J.,Wong Hio,Galicia Nicole,Pacheco Glenn,Van Vleet Jeremy,Giaramita Alexander,Fong Sylvia,Roy Sushmita M.,Hague Chuck,Lawrence Roger,Bullens Sherry,Christianson Terri M.,d'Azzo Alessandra,Crawford Brett E.,Bunting Stuart,LeBowitz Jonathan H.,Yogalingam Gouri^ORCID

Publisher

Elsevier BV

Subject

Cell Biology,Molecular Biology,Biochemistry

Reference40 articles.

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