Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry-Reference-Cited by-同舟云学术

Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry

Published:2002-08 Issue:2 Volume:113 Page:112-119
ISSN:0002-9343
Container-title:The American Journal of Medicine
language:en
Short-container-title:The American Journal of Medicine

Author:

Weinreb Neal J,Charrow Joel,Andersson Hans C,Kaplan Paige,Kolodny Edwin H,Mistry Pramod,Pastores Gregory,Rosenbloom Barry E,Scott C.Ronald,Wappner Rebecca S,Zimran Ari

Publisher

Elsevier BV

Subject

General Medicine

Reference43 articles.

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2. Glucosylceramide lipidoses;Beutler,1995

3. Enzyme therapy in Gaucher disease type 1;Grabowski;Ann Intern Med,1995

4. Replacement therapy for inherited enzyme deficiency;Barton;N Engl J Med,1991

5. Enzyme replacement therapy in Gaucher disease type 1;Rosenthal;Pediatrics,1995

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