Impact of enzyme replacement therapy and hematopoietic stem cell therapy on growth in patients with Hunter syndrome-Reference-Cited by-同舟云学术

Impact of enzyme replacement therapy and hematopoietic stem cell therapy on growth in patients with Hunter syndrome

Published:2014 Issue: Volume:1 Page:184-196
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Patel Pravin,Suzuki Yasuyuki,Tanaka Akemi,Yabe Hiromasa,Kato Shunichi,Shimada Tsutomu,Mason Robert W.,Orii Kenji E.,Fukao Toshiyuki,Orii Tadao,Tomatsu Shunji

Funder

Austrian MPS Society

International Morquio Organization (Carol Ann Foundation)

Japanese MPS Family Society

NIH

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology

Reference32 articles.

1. Mucopolysaccharidosis type II;Scarpa,2007

2. Enzyme replacement therapy and substrate reduction therapy in lysosomal storage disorders with neurological expression;Valayannopoulos;Handb. Clin. Neurol.,2013

3. Incidence of the mucopolysaccharidoses in Western Australia;Nelson;Am. J. Med. Genet. A,2003

4. Cumulative incidence rates of the mucopolysaccharidoses in Germany;Baehner;J. Inherit. Metab. Dis.,2005

5. Incidence of the mucopolysaccharidoses in Taiwan, 1984–2004;Lin;Am. J. Med. Genet. A,2009

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