Long-term follow-up of patients with type 2 and non-ambulant type 3 spinal muscular atrophy (SMA) treated with olesoxime in the OLEOS trial-Reference-Cited by-同舟云学术

Long-term follow-up of patients with type 2 and non-ambulant type 3 spinal muscular atrophy (SMA) treated with olesoxime in the OLEOS trial

Published:2020-12 Issue:12 Volume:30 Page:959-969
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Muntoni Francesco,Bertini Enrico,Comi Giacomo,Kirschner Janbernd,Lusakowska Anna,Mercuri Eugenio,Scoto Mariacristina,van der Pol W Ludo,Vuillerot Carole,Burdeska Alexander,El-Khairi Muna,Fontoura Paulo,Ives Jane,Gorni Ksenija,Reid Carol,Fuerst-Recktenwald Sabine

Publisher

Elsevier BV

Subject

Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health

Reference51 articles.

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