Gene therapy and other novel treatment approaches for Charcot-Marie-Tooth disease
Author:
Publisher
Elsevier BV
Subject
Genetics (clinical),Neurology (clinical),Neurology,Pediatrics, Perinatology and Child Health
Reference79 articles.
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2. High dosage ascorbic acid treatment in Charcot-Marie-Tooth disease type 1A: results of a randomized, double-masked, controlled trial;Lewis;JAMA Neurol,2013
3. Ascorbic acid in Charcot-Marie-Tooth disease type 1A (CMT-TRIAAL and CMT-TRAUK): a double-blind randomised trial;Pareyson;Lancet Neurol,2011
4. Oral high dose ascorbic acid treatment for one year in young CMT1A patients: a randomised, double-blind, placebo-controlled phase II trial;Verhamme;BMC Med,2009
5. Challenges in treating charcot-marie-tooth disease and related neuropathies: current management and future perspectives;Pisciotta;Brain Sci,2021
Cited by 11 articles. 订阅此论文施引文献 订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献
1. Current Treatment Methods for Charcot–Marie–Tooth Diseases;Biomolecules;2024-09-09
2. Efficient data labeling strategies for automated muscle segmentation in lower leg MRIs of Charcot-Marie-Tooth disease patients;PLOS ONE;2024-09-06
3. Navigating the Landscape of CMT1B: Understanding Genetic Pathways, Disease Models, and Potential Therapeutic Approaches;International Journal of Molecular Sciences;2024-08-26
4. Charcot-Marie-Tooth Disease With Leukodystrophy: An Atypical Presentation;Cureus;2024-07-11
5. Gene therapies for CMT neuropathies: from the bench to the clinic;Current Opinion in Neurology;2024-06-14
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