Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial-Reference-Cited by-同舟云学术

Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial

Published:2024-09 Issue:9 Volume:23 Page:871-882
ISSN:1474-4422
Container-title:The Lancet Neurology
language:en
Short-container-title:The Lancet Neurology

Author:

Zielen Stefan,Crawford Thomas,Benatti Luca,Magnani Mauro,Kieslich Matthias,Ryan Monique,Meyts Isabelle,Gulati Sheffali,Borgohain Rupam,Yadav Ravi,Pal Pramod,Hegde Anaita,Kumar Suresh,Venkateswar Anand,Udani Vrajesh,Vinayan Kollencheri P,Nissenkorn Andreea,Fazzi Elisa,Leuzzi Vincenzo,Stray-Pedersen Asbjørg,Pietrucha Barbara,Pascual Samuel I,Gouider Riadh,Koenig Mary Kay,Wu Steve,Perlman Susan,Thye Dirk,Janhofer Guenter,Horn Biljana,Whitehouse William,Lederman Howard

Funder

Horizon 2020

Publisher

Elsevier BV

Reference22 articles.

1. The natural history of ataxia-telangiectasia (A-T): A systematic review;Petley;PLoS One,2022

2. Persistent DNA damage associated with ATM kinase deficiency promotes microglial dysfunction;Bourseguin;Nucleic Acids Res,2022

3. Inhibition of the cGAS-STING pathway ameliorates the premature senescence hallmarks of ataxia-telangiectasia brain organoids;Aguado;Aging Cell,2021

4. Accumulation of DNA damage and reduced levels of nicotine adenine dinucleotide in the brains of Atm-deficient mice;Stern;J Biol Chem,2002

5. Malfunctioning DNA damage response (DDR) leads to the degeneration of nigro-striatal pathway in mouse brain;Kirshner;J Mol Neurosci,2012

Cited by 1 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Lessons from the ATTeST trial in ataxia telangiectasia;The Lancet Neurology;2024-09