AAV9-mediated SH3TC2 gene replacement therapy targeted to Schwann cells for the treatment of CMT4C-Reference-Cited by-同舟云学术

AAV9-mediated SH3TC2 gene replacement therapy targeted to Schwann cells for the treatment of CMT4C

Published:2023-11 Issue:11 Volume:31 Page:3290-3307
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Georgiou Elena^ORCID,Kagiava Alexia,Sargiannidou Irene,Schiza Natasa,Stavrou Marina,Richter Jan,Tryfonos Christina,Heslegrave Amanda,Zetterberg Henrik,Christodoulou Christina,Kleopa Kleopas A.^ORCID

Funder

Charcot-Marie-Tooth Association

UK Dementia Research Institute

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. A clinical, electrophysiologic, neuropathologic, and genetic study of two large Algerian families with an autosomal recessive demyelinating form of Charcot-Marie-Tooth disease;Kessali;Neurol. Apr,1997

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