Preclinical studies of gene replacement therapy for CDKL5 deficiency disorder
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Published:2024-07
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ISSN:1525-0016
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Container-title:Molecular Therapy
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language:en
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Short-container-title:Molecular Therapy
Author:
Voronin Gregory, Narasimhan Jana, Gittens Jamila, Sheedy Josephine, Lipari Philip, Peters Melinda, DeMarco Steven, Cao Liangxian, Varganov Yakov, Kim Min Jung, Pear Lisset, Fotouh Eman, Sinha Supriya, Ray Balmiki, Wu Michael C., Yalamanchili Padmaja, Southgate Christopher, Pick Joseph, Saadipour Khalil, Jung Stephen, Lee Jeanee, Mollin Anna, Welch Ellen M., Wu Zhijian, Weetall MarlaORCID
Funder
PTC Therapeutics Inc
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