Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies-Reference-Cited by-同舟云学术

Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies

Published:2022-08 Issue:8 Volume:30 Page:2693-2708
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Liu Boya^ORCID,Brendel Christian,Vinjamur Divya S.,Zhou Yu,Harris Chad,McGuinness Meaghan,Manis John P.,Bauer Daniel E.,Xu Haiming,Williams David A.^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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4. Gene therapy for sickle cell disease: an update;Demirci;Cytotherapy,2018

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