Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference62 articles.
1. Gene therapy for beta-hemoglobinopathies;Cavazzana;Mol. Ther.,2017
2. Gene therapy for beta-hemoglobinopathies: milestones, New therapies and challenges;Ghiaccio;Mol. Diagn. Ther.,2019
3. Gene therapy of hematological disorders: current challenges;Al-Saif;Gene Ther.,2019
4. Gene therapy for sickle cell disease: an update;Demirci;Cytotherapy,2018
5. Genetic treatment of a molecular disorder: gene therapy approaches to sickle cell disease;Hoban;Blood,2016
Cited by 10 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Effects of Mithramycin on BCL11A Gene Expression and on the Interaction of the BCL11A Transcriptional Complex to γ-Globin Gene Promoter Sequences;Genes;2023-10-11
2. Gene Therapy for Hemoglobinopathies;Human Gene Therapy;2023-09-01
3. CRISPR-Cas9 Editing of the HBG1 and HBG2 Promoters to Treat Sickle Cell Disease;New England Journal of Medicine;2023-08-31
4. Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies;Molecular Therapy - Nucleic Acids;2023-06
5. Fetal Hemoglobin Regulation in Beta-Thalassemia;Hematology/Oncology Clinics of North America;2023-04
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3