Respiratory Needs in Patients with Type 1 Spinal Muscular Atrophy Treated with Nusinersen-Reference-Cited by-同舟云学术

Respiratory Needs in Patients with Type 1 Spinal Muscular Atrophy Treated with Nusinersen

Published:2020-04 Issue: Volume:219 Page:223-228.e4
ISSN:0022-3476
Container-title:The Journal of Pediatrics
language:en
Short-container-title:The Journal of Pediatrics

Author:

Sansone Valeria A.,Pirola Alice^ORCID,Albamonte Emilio,Pane Marika,Lizio Andrea,D'Amico Adele,Catteruccia Michela,Cutrera Renato,Bruno Claudio,Pedemonte Marina,Messina Sonia,Rao Fabrizio,Roma Elisabetta,Salmin Francesca,Coratti Giorgia^ORCID,Di Bari Alessandra,De Sanctis Roberto,Pera Carmela Maria,Sframeli Maria,Piastra Marco,Macagno Francesco,Vita Giuseppe,Bertini Enrico,Mercuri Eugenio

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology, and Child Health

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3. Spontaneous breathing pattern as respiratory functional outcome in children with spinal muscular atrophy (SMA);LoMauro;PLoS One,2016

4. Diagnosis and management of spinal muscular atrophy: part 2: pulmonary and acute care; medications, supplements and immunizations; other organ systems; and ethics;Finkel;Neuromuscul Disord,2018

5. Observational study of spinal muscular atrophy type I and implications for clinical trials;Finkel;Neurology,2014

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