Gaucher disease: lessons from a decade of therapy
Author:
Publisher
Elsevier BV
Subject
Pediatrics, Perinatology and Child Health
Reference9 articles.
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2. Current issues in diagnosis and treatment. NIH Technology Assessment Panel on Gaucher Disease;Gaucher disease;JAMA,1996
3. Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry;Weinreb;Am J Med,2002
4. Enzyme therapy in Gaucher disease type 1: dosage efficacy and adverse effects in 33 patients treated for 6 to 24 months;Pastores;Blood,1993
5. The health-related quality of life of adults with Gaucher' disease receiving enzyme replacement therapy: results from a retrospective study;Damiano;Qual Life Res,1998
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