Therapeutic possibilities in the autosomal recessive limb-girdle muscular dystrophies
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical),Neurology (clinical),Pharmacology
Link
http://www.springerlink.com/index/pdf/10.1016/j.nurt.2008.08.003
Reference103 articles.
1. Vainzof M, Ayub-Guerrieri D, Onofre PC, et al. Animal models for genetic neuromuscular diseases. J Mol Neurosci 2008;34: 241–248.
2. Bassett DI, Currie PD. The zebrafish as a model for muscular dystrophy and congenital myopathy. Hum Mol Genet 2003;12(Spec No 2): R265-R270.
3. Guyon JR, Steffen LS, Howell MH, Pusack TJ, Lawrence C, Kunkel LM. Modeling human muscle disease in zebrafish. Biochim Biophys Acta 2007;1772: 205–215.
4. Kunkel LM, Bachrach E, Bennett RR, Guyon J, Steffen L. Diagnosis and cell-based therapy for Duchenne muscular dystrophy in humans, mice, and zebrafish. J Hum Genet 2006;51: 397–406.
5. Sampaolesi M, Torrente Y, Innocenzi A, et al. Cell therapy of alpha-sarcoglycan null dystrophic mice through intra-arterial delivery of mesoangioblasts. Science 2003;301: 487–492.
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