Increased CFTR expression and function from an optimized lentiviral vector for cystic fibrosis gene therapy
Author:
Funder
National Institutes of Health
Cystic Fibrosis Foundation
Center for Gene Therapy, University of Iowa
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference80 articles.
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4. Repeated aerosolized AAV-CFTR for treatment of cystic fibrosis: a randomized placebo-controlled phase 2B trial;Moss;Hum. Gene Ther.,2007
5. Efficient and persistent gene transfer of AAV-CFTR in maxillary sinus;Wagner;Lancet,1998
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