Efficient CRISPR-Cas9-Mediated Gene Ablation in Human Keratinocytes to Recapitulate Genodermatoses: Modeling of Netherton Syndrome-Reference-Cited by-同舟云学术

Efficient CRISPR-Cas9-Mediated Gene Ablation in Human Keratinocytes to Recapitulate Genodermatoses: Modeling of Netherton Syndrome

Published:2020-09 Issue: Volume:18 Page:280-290
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Gálvez Victoria,Chacón-Solano Esteban,Bonafont Jose,Mencía Ángeles,Di Wei-Li,Murillas Rodolfo,Llames Sara,Vicente Asunción,Del Rio Marcela,Carretero Marta,Larcher Fernando

Funder

Ministerio de Economía, Industria y Competitividad, Gobierno de España

European Regional Development Fund

Instituto de Salud Carlos III

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference39 articles.

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3. Systematic comparison of CRISPR/Cas9 and RNAi screens for essential genes;Morgens;Nat. Biotechnol.,2016

4. Clinically relevant correction of recessive dystrophic epidermolysis bullosa by dual sgRNA CRISPR/Cas9-mediated gene editing;Bonafont;Mol. Ther.,2019

5. Ex-vivo gene therapy restores LEKTI activity and corrects the architecture of Netherton syndrome-derived skin grafts;Di;Mol. Ther.,2011

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