Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo-Reference-Cited by-同舟云学术

Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo

Published:2023-09 Issue: Volume:30 Page:546-557
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Asperti Claudia,Canarutto Daniele,Porcellini Simona,Sanvito Francesca,Cecere Francesca,Vavassori Valentina,Ferrari Samuele,Rovelli Elisabetta,Albano Luisa,Jacob Aurelien,Sergi Sergi Lucia,Montaldo Elisa,Ferrua Francesca,González-Granado Luis Ignacio,Lougaris Vassilios,Badolato Raffaele,Finocchi Andrea,Villa Anna,Radrizzani Marina,Naldini Luigi^ORCID

Funder

Fondazione Telethon

Ministero della Salute

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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