Mitigation of cerebellar neuropathy in globoid cell leukodystrophy mice by AAV-mediated gene therapy-Reference-Cited by-同舟云学术

Mitigation of cerebellar neuropathy in globoid cell leukodystrophy mice by AAV-mediated gene therapy

Published:2015-10 Issue:1 Volume:571 Page:81-90
ISSN:0378-1119
Container-title:Gene
language:en
Short-container-title:Gene

Author:

Lin Dar-Shong,Hsiao Chung-Der,Lee Allan Yueh-Luen,Ho Che-Sheng,Liu Hsuan-Liang,Wang Tuen-Jen,Jian Yuan-Ren,Hsu Jui-Cheng,Huang Zon-Darr,Lee Tsung-Han,Chiang Ming-Fu

Funder

Ministry of Science and Technology, Taiwan

Mackay Memorial Hospital

Publisher

Elsevier BV

Subject

Genetics,General Medicine

Reference51 articles.

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2. Molecular genetics of Krabbe disease (globoid cell leukodystrophy): diagnostic and clinical implications;Wenger;Hum. Mutat.,1997

3. Analysis of galactosylsphingosine (psychosine) in the brain;Igisu;J. Lipid Res.,1984

4. Psychosine, the cytotoxic sphingolipid that accumulates in globoid cell leukodystrophy, alters membrane architecture;Hawkins-Salsbury;J. Lipid Res.,2013

5. Psychosine-induced apoptosis in a mouse oligodendrocyte progenitor cell line is mediated by caspase activation;Zaka;Neurosci. Lett.,2004

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