Gene Therapy for Muscular Dystrophy: Moving the Field Forward
Author:
Publisher
Elsevier BV
Subject
Clinical Neurology,Developmental Neuroscience,Neurology,Pediatrics, Perinatology, and Child Health
Reference56 articles.
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4. Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping;Goyenvalle;Mol Ther,2010
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