Cystic fibrosis 2019: Year in review
Author:
Publisher
Elsevier BV
Subject
Pulmonary and Respiratory Medicine,Pediatrics, Perinatology, and Child Health
Reference24 articles.
1. Elexacaftor-tezacaftor-ivacaftor for cystic fibrosis with a single Phe508del allele;Middleton;N Engl J Med,2019
2. Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial;Heijerman;Lancet,2019
3. Lumacaftor-ivacaftor in patients with cystic fibrosis homozygous for Phe508del CFTR;Wainwright;N Engl J Med,2015
4. A CFTR corrector (lumacaftor) and a CFTR potentiator (ivacaftor) for treatment of patients with cystic fibrosis who have a phe508del CFTR mutation: a phase 2 randomised controlled trial;Boyle;Lancet Respir Med,2014
5. Tezacaftor-Ivacaftor In Patients With Cystic Fibrosis Homozygous for Phe508del;Taylor-Cousar;N Engl J Med,2017
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2. Patient and Caregiver Perceptions of Airway Clearance Methods Used for Cystic Fibrosis;Canadian Respiratory Journal;2023-07-28
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